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Health Dictionary

Reliable, easy-to-read patient information on common medical conditions — written in plain language, free of jargon, and grounded in current evidence. Browse the most frequent diagnoses, understand what they mean for everyday life, and learn which steps and questions help you have a focused conversation with your doctor.

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Cystic fibrosis future or investigational therapies

Introduction

Overview

Overview

In cystic fibrosis therapies under investigation include prophylactic ursodiol therapy; CF corrector VX-661; inhaled dry powder mannitol and CFTR gene therapy.

future or investigational therapies

future or investigational therapies

In cystic fibrosis therapies under investigation include:^[1]

Prophylactic ursodiol therapy
CF corrector VX-661
Inhaled dry powder mannitol
CFTR gene therapy

References

References

↑ “Cystic Fibrosis and Congenital Absence of the Vas Deferens – GeneReviews® – NCBI Bookshelf”.

Editor-In-Chief: C. Michael Gibson, M.S., M.D. [1]; Associate Editor(s)-in-Chief: Shaghayegh Habibi, M.D.[2]